Multi-stakeholder Symposium on Improving Patient Access to Rare Disease Therapies
An exceptional two-day event not to be missed!
24 - 25 February 2016
No new on-site registrations will be accepted
EURORDIS and partners will bring together industry, patient leaders, academics, regulators and payers to discuss the current state of play and how to shape a more effective way to address value determination, appraisal, pricing and reimbursement of orphan medicines. In line with the EURORDIS Round Table of Companies, this symposium aims to improve patients' access to rare disease therapies throughout Europe.
This meeting on the topic of HTA is envisaged as a two-stage process, with a second symposium in 2017 on a more consensual approach to the new solutions discussed throughout 2016. For this 1st meeting, the overarching aim is to gain common understanding and agreement on the determinants of value, and of the assessment and appraisal methods for orphan medicinal products, by:
Bringing all participants to a common understanding of issues/challenges of access to rare disease therapies (webinar/pre-reads to be circulated before meeting);
Sharing existing and new processes to recognise which ones work best;
In view of the 2017 symposium, agreeing on a structured approach forward and a set of solutions to explore.
Professor of Health Economics
Ri De Ridder
Director-General of Healthcare
Evidence Based Health Policy Consultant
Director, Healthcare Policy and External Affairs Europe
Public Policy and External Affairs
Sobi - Swedish Orphan Biovitrum AB
Senior Director European Government Relations and Public Policy
Co-chair EFPIA - EuropaBio Task Force
Senior Director, International Policy
Therapeutic Development Director
Yann Le Cam
Chief Executive Officer
co-chair EFPIA - EuropaBio Task Force
Director Public Affairs
Genzyme Europe BV
Advisors to the Programme Committee:
Treatment Information and Access Director / Health Policy Advisor
Head of Office – Orphan Medicinal Products
European Medicines Agency (EMA)
ADAPT SMART consortium (EMA)
Director Regulatory Affairs
Head of the Business Contact Centre & International Affairs
National Health Care Institute (former CVZ)
European Genetic Alliances Network (EGAN)
UK Thalassaemia Society
6. Hotel & Travel Information
EURORDIS has booked a block of rooms and has negotiated special rates at the Hotel Le Plaza for the nights of 24 and 25 February 2016. If you wish to make a reservation at the Hotel Le Plaza, please contact the reservation department directly (Tel. +32 2 278 01 00 / email@example.com).
Single occupancy: 195 Euros per night including breakfast*
Double occupancy: 224 Euros per night including breakfast* *City Tax is not included in the room rate - a supplement of 9.85 € per room per night will be applied
Details of other hotels close to the venue will be provided here soon.
Date: Thursday 4th February 2016, from 15.00 to 16.00 CET Moderator: Julia Chamova from EUnetHTA Co-presented by Conor Teljeur from EUnetHTA & François Houÿez, Treatment Information and Access Director at EURORDIS.