How to proceed

This website section explains how your physician can request authorisation to prescribe to you a medicine on a compassionate basis. As the procedure varies from one country to another, different examples will be cited. Refer to the section on Resources to find out how to proceed in your country, when the information is available.


Your doctor may contact the company to verify if the medicine is available for compassionate use

The process to follow when no one has requested the medicine on a compassionate use basis before


Your national competent authority has already accepted a Compassionate Use Programme

The process when a Compassionate Use Programme is already in place


The specific case of a named-patient Compassionate Use Programme

Compassionate use on a named-patient basis is another possibility for early access to a medicinal product


Ten tips for industry when planning a CUP

Not all companies organise their Compassionate Use Programmes in the same way.  Below are some tips, based upon our experience.

The voice of rare disease patients in EuropeEURORDIS The international voice of people living with rare diseasesRare Disease International Bringing together patients, families and experts to share experiences in a moderated multi-language forum. RareConnect The Rare Barometer Programme is a EURORDIS initiative that carries out surveys to transform rare disease patients' experiences into figures and facts that can be shared with decision-makers.Rare Barometer An international awareness raising campaign taking place on the last day of February each year, Rare Disease Day is a EURORDIS initiativeRare Disease Day Join the largest gathering of rare disease stakeholders across Europe, at the biennial European Conference on Rare Diseases and Orphan Products. ECRD is a EURORDIS initiativeEuropean Conference on Rare Diseases