Resources

Useful services: where you can learn more about Compassionate Use Programmes.

 

Links to national authority websites

Public information on compassionate use programmes will be available soon.  See below for who to contact in your national authority

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The European Register of Clinical Trials (EudraCT-R) and other online sources

EudraCT Register is the database of all clinical trials authorised in Europe, and has information on Compassionate Use Programmes

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The website of the National Institutes of Health in the USA

The NIH database of clinical trials provides more information on Compassionate Use Programmes

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The website of the European Medicines Agency (EMA)

The European Medicines Agency plays a role in defining who can benefit from compassionate use

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Links to Help Lines: How can I find a Compassionate Use Programme for my disease - can anyone help?

The European Network of Rare Diseases Help Lines can assist you in finding the information you need

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Compassionate Use Glossary

Terms you may need to understand compassionate use better

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