The website of the National Institutes of Health in the USA

The NIH database of clinical trials provides more information on Compassionate Use Programmes

The NIH database of clinical trials database can be searched at:

This website is very similar to the EudraCT register; it contains information on clinical trials, studies, and Compassionate Use Programmes  worldwide, including European sites.

In the USA, the equivalent term for Compassionate Use Programmes is “Expanded access studies”. You can choose this option in study type. Unlike the EU register, you cannot restrict the search to rare diseases.

Searching for compassionate use programmes in the NIH database

Searching for compassionate use programmes in the NIH database

You can also type the name of a specific disease  and see if and where compassionate use programmes are listed.

The EudraCT register has been in use since 2006


The European Register of Clinical Trials:


Page created: 30/10/2013
Page last updated: 07/11/2014
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