Michele Lipucci di Paoloa

Dr. Michele Lipucci Di Paola, scientist in Plant Biology at the University of Pisa (Italy). Since 1997 to 2006 Board Member and Former Vice-President EURORDIS, since 2002 Vice-President AVLT (Associazione Veneta Lotta alla Talassemia, Rovigo, Italy) , since 2006 Board Member PBSA (Pan-European Blood Safety Alliance), since 2000 Coordinator Research& Development and Director External Relations of THAL-LAB (Laboratory for the Development of Genetic and Pharmacogenomics Therapy of Thalassemia)/Center Biotechnology/University of Ferrara). Since 2003 to 2006 Member EMA/WGIP/COMP (European Medicines Agency/ Working Group Interested Parties/ Committee Orphan Medicinal Products), since 2009 Alternate Member.

EMA/CAT (European Medicines Agency/ Committee Advanced Therapy) representing patients' organizations. 'The promises that advanced therapies hold for the successful treatment of certain rare diseases are now closer to becoming a reality', argues Michele Lipuci Di Paola, recently appointed as the EURORDIS representative to the Committee. 'The creation of the CAT is the most important part of the process, because without it advanced therapy medicinal products could never reach the market.

The voice of rare disease patients in EuropeEURORDIS The international voice of people living with rare diseasesRare Disease International Bringing together patients, families and experts to share experiences in a moderated multi-language forum. RareConnect The Rare Barometer Programme is a EURORDIS initiative that carries out surveys to transform rare disease patients' experiences into figures and facts that can be shared with decision-makers.Rare Barometer An international awareness raising campaign taking place on the last day of February each year, Rare Disease Day is a EURORDIS initiativeRare Disease Day Join the largest gathering of rare disease stakeholders across Europe, at the biennial European Conference on Rare Diseases and Orphan Products. ECRD is a EURORDIS initiativeEuropean Conference on Rare Diseases