Patients Access to Treatment

EU level legislation and initiatives encourage the development of rare disease medicines and foster equitable access across Europe.

 

Orphan Medicine Regulation

Orphan medicines legislation aims at providing incentives for pharmaceutical companies to develop and market medicinal products to treat rare diseases.

ler mais...
 

Orphan Medicines Designation

Medicines intended for rare diseases can receive an orphan designation in the European Union and benefit from a number of regulatory incentives.

ler mais...
 

Committee for Orphan Medicinal Products (COMP)

The Committee for Orphan Medicinal Products (COMP) was created within the European Medicines Agency to review orphan designation applications.

ler mais...
 

Paediatric Committee (PDCO)

The Paediatric Committee at the European Medicines Agency provides opinions on the development of medicines for children, in accordance with Regulation (EC) 1901/2006.

ler mais...
 

Clinical Added Value of Orphan Medicinal Products Information Flow (CAVOMP-INF)

The CAVOMP-INF considers how to coordinate the respective procedures for marketing authorisation and for reimbursement decisions.

ler mais...
 

Mechanism of Coordinated Access to orphan medicinal products (MoCA)

The MoCA seeks collaborative ways to identify and assess the added value of orphan medicinal products.

ler mais...
 

Transparency Directive

Transparency Directive 89/105/EEC is being revised in order to streamline, reduce delays and improve transparency in the Member State decision process for the pricing and reimbursement of medicines.

ler mais...
 
 
A voz das pessoas com doenças raras na EuropaEURORDIS A voz internacional das pessoas com doenças raras, Rare Diseases Internacional, é uma iniciativa da EURORDISRare Disease International Reúne doentes, famílias e especialistas para partilhar experiências num fórum multilinguístico. RareConnect O programa Rare Barometer é uma iniciativa da EURORDIS para a realização de inquéritos para transformar a experiência das pessoas com doenças raras em números e factos que podem ser partilhados com os responsáveis pela tomada de decisões.Rare Barometer An international awareness raising campaign taking place on the last day of February each year, Rare Disease Day is a EURORDIS initiativeRare Disease Day Adira ao maior encontro europeu das partes interessadas no âmbito das doenças raras na Conferência Bienal Europeia sobre Doenças Raras e Produtos Órfãos. A ECRD é uma iniciativa da EURORDISEuropean Conference on Rare Diseases