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The use of real world data for regulatory purposes in the rare diseases settingNovembro 2022Read more
Identifying obstacles hindering the conduct of academic‑sponsored trials for drug repurposing on rare‑diseases: an analysis of six use casesSetembro 2022Read more
Paediatric Inflammatory Bowel Disease: A Multi-Stakeholder Perspective to Improve Development of Drugs for Children and AdolescentsSetembro 2022Read more
Factsheets and infographics
Juggling care and daily life: The balancing act of the rare disease community – InfographicFevereiro 2023Read More
EURORDIS’ Proposal on the Revision of the Orphan Medicinal Products and Paediatric RegulationNovembro 2022Read More